Unlocking the Potential of Gene Therapy
Battling Genetic Diseases With the Body’s Blueprint
Genes serve as the intricate blueprints guiding the body’s cellular functions; however, when these instructions go awry, disease occurs. Gene therapy harnesses the building blocks of life to treat genetic diseases at their source. Modified viruses and cutting-edge technologies deliver therapeutic genes directly to cells or tissues, correcting genetic abnormalities at their root.
One of the most groundbreaking advancements in this field is the adeno-associated virus (AAV), a safe and effective delivery system for genetic material that offers precise control, immense potential for combatting an array of diseases, and minimal risk of replication within the body. With its proven track record and FDA-approved status, AAV is a beacon of hope in the realm of genetic medicine, driving therapeutic discoveries and transforming the landscape of treatment options for patients worldwide.
AAV Gene Therapy: Powering Possibilities
At AskBio, we’re harnessing advanced AAV technology to revolutionize gene therapy and enhance patients’ lives. Through precise gene delivery, we’re pioneering targeted treatments for a wide range of genetic diseases. The groundbreaking work of our co-founder, Dr R. Jude Samulski, has positioned us at the forefront of innovation in this field.
AskBio is more committed than ever to our mission of improving lives—striving every day to make meaningful impact for the communities we serve.
What are Genetic Disorders?
There are several types of genetic diseases that result from missing genes or mutations in the genome. Some symptoms are visible after birth, while others appear later in life.
How We Bring Gene Therapeutics to Life
Our world-class team of researchers and scientists is working diligently to eradicate genetic diseases.
