Transforming medicine and changing lives
November 19, 2020
AskBio and Selecta Biosciences Receive Orphan Drug Designation for MMA-101 to Treat Methylmalonic AcidemiaThe FDA has granted orphan drug and rare pediatric disease designations to AskBio's gene therapy, MMA-101, for the treatment of methylmalonic acidemia. ...read the news
We are on a never-ending quest to advance genetic technology
and life-saving AAV gene therapy
In 1984, Dr. Jude Samulski, one of AskBio’s visionary founders, asked if a virus could be used to erase genetic disease. Discovering the answer cleared the path for historic advances in genetic medicine, and AskBio is leading the way.
Revolutionizing gene therapy
Cures for life-altering genetic diseases depend on new technology to lower the cost of treatment and increase supply for every patient who needs it.
Changing lives
Our clinical pipeline is the direct result of listening to patients, their families, their care teams and disease-advocacy organizations.
Putting patient care first
The voices of those affected by genetic disorders drive everything we do. They propel our research and the urgent need to find cures.
Work with us
Advancing research
Today’s genetic discoveries are some of the most awe-inspiring advances in medical history. We welcome collaboration with innovative minds in genetic R&D.
Building careers
Help transform the face of healthcare with life-changing gene therapy. Every life enriched by our scientific advancements is a result of people like you.
