Transforming medicine and changing lives


June 23, 2020

AAV Gene Therapy Pioneer Jude Samulski Develops Proprietary Regulated Gene Editing System

Technology brings tgether benefits of AAV and CRISPR while minimizing negative effects that occur during gene editing the news

We are on a never-ending quest to advance genetic technology

and life-saving AAV gene therapy

In 1984, Dr. Jude Samulski, one of AskBio’s visionary founders, asked if a virus could be used to erase genetic disease. Discovering the answer cleared the path for historic advances in genetic medicine, and AskBio is leading the way.

Learn about AskBio »

gene therapy

Revolutionizing gene therapy

Cures for life-altering genetic diseases depend on new technology to lower the cost of treatment and increase supply for every patient who needs it.

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Clinical Pipeline

Changing lives

Our clinical pipeline is the direct result of listening to patients, their families, their care teams and disease-advocacy organizations.

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Putting patient care first

The voices of those affected by genetic disorders drive everything we do. They propel our research and the urgent need to find cures.

For Patients »

Work with us

Advancing research

Today’s genetic discoveries are some of the most awe-inspiring advances in medical history. We welcome collaboration with innovative minds in genetic R&D.

Building careers

Help transform the face of healthcare with life-changing gene therapy. Every life enriched by our scientific advancements is a result of people like you.


Gene Therapy for Neurological Disorders Europe

Jul 15

We’re speaking at the Gene Therapy for Neurological Disorders Europe conference, which will be held as a virtual meeting on July 15, 2020. The conference unites industry leaders to help them overcome translational challenges and successfully bring CNS gene therapy candidates into the clinic.