AskBio in the News
Press Releases
As a world-leading gene therapy company, we are continuously advancing AAV therapeutics, discovering new technology, forging new research collaborations, and adding amazing talent to our team.
First Patient Dosed with Gene Therapy in Phase 1/2 Study of ACTUS-101 in Patients with Pompe Disease
February 9, 2022
Bayer-owned AskBio will shift focus toward its doggybone DNA in restructure with Touchlight
Endpoints News
December 16, 2021
Innovation in rAAV gene therapy is a need: AAV capsids
Cell & Gene Therapy Insights
September 17, 2021
On “Optionality,” Exits and Giving Science the Best Chance to Save Lives
Southeast Life Sciences
July 15, 2021
Gene therapy delivered to the brain shows promise in children with rare neurodegenerative disease
FierceBiotech
March 12, 2021
AskBio Makes Next Leadership Play; Selects Bayer’s Guru Ramamurthy as Finance Chief
Endpoints News
February 4, 2021
‘Gene Therapy at an Inflection Point’: Kathy High on Her New Perch at AskBio and the Field’s Future
Endpoints News
January 28, 2021
Bayer and AskBio Expand Grand Gene Therapy Ambitions with New Parkinson’s Program, Top Scientist
Endpoints News
January 12, 2021
Spark Co-founder Kathy High Joins AskBio, Helping Steer Bayer’s Gene Therapy Push
Endpoints News
November 27, 2020
Making Gene Therapies Accessible to Patients with Ultra-Rare Conditions
RARECast | Global Genes Podcast
October 27, 2020
AskBio to be Hiring ‘Across the Board,’ CEO Says After $4B Deal with Bayer
WRAL Techwire
October 26, 2020
Bayer Buys a Biotech ‘Race Horse’ with a $4B Deal — $2B in Cash — Aimed at Going Big into Gene Therapy
Endpoints News
September 22, 2020
Axovant Partners with Viralgen to Scale Production of Its AAV Gene Therapies
BioPharma Journal
August 12, 2020
Inc. 5000 2020: Introducing the 5,000 Fastest-Growing Private Companies in America
Inc. Magazine
August 3, 2020
From Science Fiction to Reality | Jude Samulski Honored in 2020 PharmaVOICE 100
PharmaVOICE
July 20, 2020
Researchers Hope Experimental Gene Therapy Is an Answer to a Fatal Genetic Disorder
7-minute listen
NPR | All Things Considered
June 24, 2020
Gene-editing Breakthrough? AskBio’s Jude Samulski Seeks Patent for New System
WRAL Techwire
April 28, 2020
AskBio Takes Over French Gene Therapy Company to Treat Alzheimer’s and Huntington’s
Labiotech EU
April 10, 2020
RTP-based AskBio Taps Former Histogenics Exec as New Chief Business Officer
WRAL Techwire
March 17, 2020
Big Pharma Shied Away from Gene Therapy for Years. Academia Picked Up the Slack.
BioPharma Dive
February 5, 2020
AskBio Initiates Phase I Trial of Gene Therapy for Heart Failure
Clinical Trials Arena
February 3, 2020
AskFirst: AskBio’s New Gene Therapy Program for Clinical Trial Patients
WRAL TechWire
December 19, 2019
Triangle-based AskBio to Pay up to $240M for Rights to Use Gene Therapy Technology
WRAL TechWire
December 3, 2019
New Decade, New Disruption: Cell and Gene Therapy to Eradicate Genetic Diseases
Medical Expo
December 3, 2019
SQZ Biotech and AskBio Collaborate to Overcome AAV Immunogenicity
Manufacturing Chemist
October 24, 2019
Triangle Life Science Exec Sheila Mikhail Shines as ‘Northstar’ Award Winner
WRAL TechWire
August 23, 2019
Pfizer’s $500M investment in Sanford highlights NC’s growth in gene therapy
News & Observer
July 09, 2019
Cover Story: AskBio’s Tumultuous Ride to Achieve Unicorn Status
Triangle Business Journal
May 7, 2019
How This Promising Gene Therapy for a Rare Neuromuscular Disease Was Fueled by Passionate Parents and a Dog
Genetic Literacy Project
Let’s connect at an upcoming event. Check out the conferences and events we are attending and where we are speaking.
Upcoming Events
There are no upcoming events.
Past Events
Advanced Therapies Week
Advanced Therapies Week is the destination for anyone developers, investors or those interested in cell and gene therapies and tissue engineered products. Throughout the week, the organizers be host a variety of networking events, focused roundtables and content sessions designed to help biotechs advance along their commercialization journey.Speaker: Sheila Mikhail, CEO & Co-Founder, AskBioPresentation & Q&A Panel
Tales from the Trenches
AskBio’s Sheila Ann Mikhail joined Matter’s Tales from the Trenches to share her entrepreneurial journey, her perseverance and vision for AskBio and lessons learned throughout her career.
Synthetic Biology Based Therapeutics Summit
AskBio’s Graham Whyteside, PhD, Director, Platform R&D, AskBio Europe, spoke at the Synthetic Biology-Based Therapeutic Summit on Advancing Synthetic Promoter Design.
Women in Biopharma
What does it take to shatter the glass ceiling in biopharma R&D? Calls to diversify the biopharma industry have grown louder over the last year, and in response, more companies have made laudable efforts to address the issue. AskBio’s Sheila Mikhail sat down with other leaders from across the biopharma industry to discuss breaking the glass ceiling, the limitations of existing gender diversity programs, and what comes next.
Cell & Gene Meeting on the Mesa
Pre-Recorded Company Presentation by Sheila Mikhail, CEO & Co-Founder, AskBio
NCBIO 27th Annual Meeting
More than 200 NCBIO members and invited guests come together to enjoy a program of speakers and panels addressing current topics of importance to the industry. Keynote speaker Jude Samulksi, Ph.D., President and CSO of AskBio will share about his start in North Carolina, current issues and what comes next in the biotechnology space.
Chardan 5th Annual Genetic Medicines Virtual Conference
Company Presentation (Fireside Chat Format)
BioProcess International and Cell & Gene Therapy Manufacturing & Commercialization US 2021
Dual Dialogue – Anatomy of an Acquisition: Bayer and AskBio
11th Annual World Orphan Drug Congress
The World Orphan Drug Congress has become the industry defining meeting on Advanced Therapies for rare diseases, featuring discussions on clinical development, manufacturing and commercialization of cell and gene therapies, as well the annual gathering for artificial intelligence and digital health solutions transforming the rare disease industry.
2021 STAT Breakthrough Science Summit
The 2021 STAT Breakthrough Science Summit will take you inside these innovations, examining how they’re being developed, adopted, and paid for. We’ll also take a look at the breakthroughs that haven’t yet hit the market, but have the potential to redefine health and medicine in the years to come.
BIO International Convention — BIO Digital
For 2021, the BIO International Convention will be held virtually as BIO Digital. BIO Digital will feature sessions on key sessions, including a discussion on gene therapy, including an industry panel on new approaches and challenges to developing and delivering genetic medicines.
Gene Therapy for Muscular Disorders
The first industry-dedicated Gene Therapy for Muscular Disorders Summit will focus on overcoming the translational and clinical challenges of developing genetic therapies targeting muscular disorders, including Pompe Disease and Limb-Girdle Muscular Dystrophy (LGMD).
East Coast CNS Therapeutics Xchange 2021
The East Coast CNS Therapeutics Xchange 2021 brings together executives from pharma and biotech to address and find solutions to the key issues faced in developing CNS therapies.
Advanced Therapies Congress & Expo 2021
The Advanced Therapies Congress & Expo 2021 is dedicated to commercialization of cell and gene therapies and regenerative medicines.
ASGCT 2021 | Virtual Meeting
We’re looking forward to the ASGCT 2021 Virtual Meeting being held held May 11-14, 2021. We have a number of presentations and sessions scheduled.
Gene Therapy Europe 2021
Join us at Gene Therapy Europe, an online congress from May 5-6, 2021 that will feature in-depth discussions on advanced analytical strategies and next-gen technologies to progress gene therapy development from discovery to clinical stages.
2021 Cell & Gene Meeting on the Mediterranean
Tune into our on-demand sessions. David Venables, President, AskBio Europe, delivers the company presentation, and Kathy High, President, Therapeutics, is a panelist for “Large Cap Cell and Gene Therapy Strategies.”
BioProcess International U.S. West 2021
Andy Holt, EVP, Commercial Development, will present “Platform Development in AAV Manufacturing: Cost & Timeline Impact on Clinical Development” on March 30 (1:15-1:35pm PDT) at the BioProcess International U.S. West 2021 conference.
CED Venture Connect 2021
Join AskBio CTO Josh Grieger on March 23 at CED Venture Connect 2021 for the Founders Discussion: Viral Vector Manufacturing in RTP.
BIO Europe Spring 2021
AskBio CEO Sheila Mikhail is a panelist for “Patient-Centered Drug Development in an Age of Cell and Gene Therapies,” which is available on demand throughout BIO Europe Spring.
9th Neurodegenerative Drug Development Summit
Join Dr. Krys Bankiewicz for the Emerging Gene Therapy Technology for Neurodegenerative Diseases workshop at the 9th Neurodegenerative Drug Development Summit on February 23, 2021.
4th Annual Gene Therapy for Rare Disorders
Join us at the 4th Annual Gene Therapy for Rare Disorders conference, which will be held as a virtual event from February 22-25, 2021. AskBio’s Dr. David Favre will present “Immunotherapeutic Interventions” on Feb. 25 at 1:30pm ET.
WORLDSymposium 2021
AskBio is an exhibitor at WORLDSymposium 2021, which will be held as a virtual event from February 8-12, 2021.
RE(ACT) Congress & IRDiRC Conference
Join gene therapy expert Nathalie Cartier-Lacave for the Advanced Therapies panel at the RE(ACT) Congress & IRDiRC Conference, which will be held as a virtual meeting from January 13-15, 2021.
Biotech Showcase 2021
Join AskBio CEO and co-founder Sheila Mikhail and Marianne De Backer, EVP, Head of Strategy, Business Development & Licensing and Executive Committee Member at Bayer AG Pharmaceuticals, for an ON DEMAND fireside chat for insights on the recent acquisition.
2nd Annual Gene Therapy for Neurological Disorders
Jude Samulski will present at the 2nd Annual Gene Therapy for Neurological Disorders conference on Dec. 10, 2020.
Chief Medical Officer Summit 360
Join us at the 8th annual Chief Medical Officer Summit, the largest gathering of physicians in biotech, to be held virtually from October 26-27, 2020.
Cell & Gene Meeting on the Mesa
AskBio is a proud sponsor of the 2020 Cell & Gene Meeting on the Mesa. CEO Sheila Mikhail will deliver a pre-recorded company presentation that will be available on demand to registered attendees from October 12-16, 2020.
Chardan 4th Annual Genetic Medicines Conference
AskBio will present at the Chardan 4th Annual Genetic Medicines Conference, which will be held as a virtual event Oct 5-6, 2020.
Longwood Healthcare Leaders Forum – Fall 2020
AskBio CEO Sheila Mikhail will participate on a panel discussion among biopharmaceutical leaders at the Longwood Healthcare Leaders Forum on Monday, October 5, 2020.
Jefferies Gene Therapy/Editing Summit 2020
AskBio CEO Sheila Mikhail will present on Friday, Oct 2, from 10:30-10:55am ET at the Jefferies Gene Therapy/Editing Summit 2020, which will be held as a virtual meeting.
Morgan Stanley Global Healthcare Conference 2020
AskBio CEO Sheila Mikhail will participate in a fireside chat at the Morgan Stanley Virtual 18th Annual Global Healthcare Conference on Friday, September 18, 2020.
Advanced Therapies Congress 2020
Join AskBio Europe President David Venables for his presentation “Maximizing Value from the Expression Cassette in Gene Therapy Product Design” on Sept. 8.
The Bioprocessing Summit 2020
We’re presenting at the 12th Annual Bioprocessing Summit, which will be held virtually from Aug 24-28, 2020.
William Blair Biotech Focus Conference 2020
AskBio CEO Sheila Mikhail will participate in a fireside chat presentation at the William Blair Biotech Focus Conference, which will be held as a virtual event August 4-6, 2020.
The Art of Gene Therapy Digital Summit
Register today for The Art of Gene Therapy Digital Summit, a live two-day event on July 28-29, 2020, and join AskBio’s Andy Holt for the Next Decade of Gene Therapy panel on July 29, 11am-12pm ET.
Gene Therapy for Neurological Disorders Europe
We’re speaking at the Gene Therapy for Neurological Disorders Europe conference, which will be held as a virtual meeting on July 15, 2020. The conference unites industry leaders to help them overcome translational challenges and successfully bring CNS gene therapy candidates into the clinic.
BIO Digital 2020
Join us, the Buzz of BIO winner, for BIO Digital 2020. We have two on-demand sessions – our company presentation and “The Role of New Technologies in Enabling Cell & Gene Therapies” panel discussion.
Jefferies Virtual Healthcare Conference
AskBio CEO Sheila Mikhail will present at the Jefferies Virtual Healthcare Conference on June 2 from 9:30-9:55am. You can also download a copy of her presentation at this link.
Chardan 4th Annual Genetic Medicines Manufacturing Summit
Join AskBio’s Tim Kelly and Andy Holt on Tuesday, May 26, for Chardan’s 4th Annual Genetic Medicines Manufacturing Summit, which will be held in a virtual format this year.
ASGCT 2020 | Virtual Meeting
We’re looking forward to ASGCT 2020, which will be held May 12-15, 2020. We have a number of oral and poster presentations scheduled.
Meeting on the Med 2020 | Barcelona
Meeting on the Med 2020 has been canceled. It will be held April 7-9, 2021 in Barcelona.
OCT Southeast 2020 | Research Triangle Park, NC
OCT Southeast 2020 has been postponed. Stay tuned for new dates.
Gene Therapy in Edinburgh
This meeting has been postponed. A new date has not yet been scheduled.
2020 MDA Clinical & Scientific Conference | Orlando
This meeting has been postponed. A new date has not yet been scheduled.
CED Venture Connect 2020
CED has postponed the Venture Connect conference and will reschedule this event for a later date in 2020.
11th Open Scientific EIP Symposium on Immunogenicity of Biopharmaceuticals | Lisbon
Join David Favre, VP Translational Medicine, for “AAV Immunogenicity: Novel Vectors & New Questions” on Feb. 18, 10am.
Alliance for Regenerative Medicine (ARM) | 2020 Cell & Gene Therapies State of the Industry
AskBio CEO Sheila Mikhail joined gene therapy leaders for the Next-Generation Gene and Cell Technologies panel. [Video]
Springboard Enterprises’ 13th Annual Winners’ Circle Dinner
AskBio CEO Sheila Mikhail was recognized at Springboard Enterprises’ 13th Annual Winners’ Circle Dinner, as the 2019 Northstar honoree.
Chardan Genetic Medicines Conference
AskBio CEO Sheila Mikhail presented at the 3rd annual Chardan Genetic Medicines Conference in New York.
Cell & Gene Meeting on the Mesa
Sheila Mikhail, CEO, of AskBio presented our differentiating capabilities, technology and therapeutic pipeline.
National Limb Girdle Muscular Dystrophy Conference
Joy Carson and Sharon Hesterlee, joined patients, families and leading stakeholders at the first-annual National Limb Girdle Muscular Dystrophy Conference in support of the LGMD patient community in Chicago.
Parent Project Muscular Dystrophy, 25th Annual Conference
AskBio’s Jude Samulski and Sharon Hesterlee joined the 25th Parent Project Muscular Dystrophy in Orlando.
Gene Therapy Panel (Alliance for Regenerative Medicine)
AskBio’s Andy Holt, VP Business Development & Manufacturing, participated on the gene therapy panel at the Alliance for Regenerative Medicine meeting held in April 2019. [Video]
The Growing Promise of Gene Therapy Approaches
Josh Grieger, PhD, Chief Technology Officer at AskBio, presented “The Growing Promise of Gene Therapy Approaches” at an NIH-hosted meeting. [Video]
Media Inquiries
We take pride in our relationships with media representatives. Our scientific experts are always available if needed for interviews and their insights.
Media Contact:
Mark Rosenberg, Corporate Communications
