AskBio in the News
Press Releases
As a world-leading gene therapy company, we are continuously advancing AAV therapeutics, discovering new technology, forging new research collaborations, and adding amazing talent to our team.
Selecta and AskBio Initiate First-in-Human Dose-Escalation Study to Evaluate ImmTOR in Gene Therapy
AskBio Adds CNS Gene Therapy Programs in Parkinson’s Disease and Multiple System Atrophy
Gene Therapy Leader Katherine High Joins AskBio as President, Therapeutics
AskBio Applauds Commencement of Pfizer’s Pivotal Trial for Duchenne Muscular Dystrophy
AskBio Welcomes Brain Neurotherapy Bio to Expand Clinical Pipeline for Neurodegenerative Diseases
AskBio CSO Jude Samulski Named 2020 Business Person of the Year by Triangle Business Journal
AskBio and Selecta Receive Orphan Drug Designation for MMA-101 to Treat Methylmalonic Acidemia
Bayer Acquires AskBio to Broaden Innovation Base in Cell and Gene Therapy
Selecta and AskBio Receive FDA Rare Pediatric Disease Designation for Methylmalonic Acidemia Gene Therapy
Kellie Sears Named AskBio Chief Human Resources Officer
AskBio Awarded £2m Scottish Enterprise R&D Grant to Help Reduce Barriers to Mainstream Gene Therapy
AskBio CSO Jude Samulski Receives 2020 Life Sciences Award from the Triangle Business Journal
AskBio Named to Inc. 5000 List of Fastest-Growing Private Companies
AskBio Appoints Michael Kranda as SVP Therapeutic Practice Leader for Its Growing CNS Portfolio
AskBio CSO Jude Samulski Named One of the Most Inspiring Leaders in Life Sciences by PharmaVOICE Magazine
Libbie Mansell Joins AskBio as SVP Regulatory Affairs
AAV Gene Therapy Pioneer Jude Samulski Develops Proprietary Regulated Gene Editing System
AskBio Appoints Tim Trost as Chief Financial Officer
AskBio Acquires BrainVectis to Expand its Clinical Pipeline for Neurodegenerative Diseases
Don Haut, PhD, Joins AskBio as Chief Business Officer
AskBio Enters Research Collaboration and Licensing Agreement with University of North Carolina (UNC) for Angelman Syndrome
Tim Kelly Joins AskBio as President of Manufacturing to Lead AAV Vector Production for Gene Therapy
CYTOO and AskBio Enter into Research Agreement to Screen Gene Therapy Candidates for Rare Muscle Disorder
AskBio Appoints Anna Tretiakova, PhD, as Senior Vice President of Product Development
AskBio Announces First Patient Dosed in Phase 1 Trial Using AAV Gene Therapy for Congestive Heart Failure
AskBio Launches AskFirst™ Patient Advocacy Program to Educate and Support Participants in Gene Therapy Clinical Trials
AskBio To Present At The 38th Annual J.P. Morgan Healthcare Conference
AskBio Licenses Rights to Selecta Biosciences’ ImmTOR™ Immune Tolerance Platform for the Treatment of Pompe Disease
AskBio Receives “Best Venture Funding” Award from Southeast BIO
SQZ Biotech and AskBio Announce Research Collaboration to Create Immune Tolerization Products for AAV Gene Therapies
Sheila Mikhail, AskBio CEO and Cofounder, Named Springboard Enterprises’ 2019 Northstar Honoree
Editas Medicine and AskBio Enter Strategic Research Collaboration to Explore In Vivo Delivery of Genome Editing Medicines to Treat Neurological Diseases
AskBio Acquires Assets from RoverMed BioSciences, Adds Nanotechnology Precision to Delivery of AAV Gene Therapeutics
Viralgen Receives cGMP Certification from European Medicines Agency
AskBio Applauds Pfizer’s Continuing Investments in Gene Therapy
AskBio Acquires Synpromics Ltd. and Expands its Gene Therapy Technology Portfolio
Selecta Biosciences Combines ImmTOR™ Platform with AskBio’s IndustryLeading Gene Therapy Platform in Strategic Partnership
Statement: Pfizer Phase 1b Clinical Trial Results
Newly Approved Spinal Muscular Atrophy Gene Therapy, Zolgensma®, Validates AskBio Gene Therapy Platform
AskBio Partners with TPG and Vida Ventures
First Patient Dosed with Gene Therapy in Phase 1/2 Study of ACTUS-101 in Patients with Pompe Disease
Asklepios BioPharmaceutical, Inc. Launches New Portfolio Company – Actus Therapeutics, Inc.
AskBio and Columbus Venture Partners Launch Gene Therapy Company Viralgen
NanoCor Announces New Data on Congestive Heart Failure Gene Therapy
Pfizer Aims To Become Industry Leader In Gene Therapy With Acquisition Of Bamboo Therapeutics, Inc.
AskBio and AveXis Finalize License
Baxter to Acquire Chatham Therapeutics
Asklepios BioPharmaceutical Enters Into A Patent License Agreement With Pfizer
Medtronic Makes Equity Investment in NanoCor Therapeutics, Inc.
February 4, 2021
‘Gene Therapy at an Inflection Point’: Kathy High on Her New Perch at AskBio and the Field’s Future
Endpoints News
January 28, 2021
Bayer and AskBio Expand Grand Gene Therapy Ambitions with New Parkinson’s Program, Top Scientist
Endpoints News
January 12, 2021
Spark Co-founder Kathy High Joins AskBio, Helping Steer Bayer’s Gene Therapy Push
Endpoints News
November 27, 2020
Making Gene Therapies Accessible to Patients with Ultra-Rare Conditions
RARECast | Global Genes Podcast
October 27, 2020
AskBio to be Hiring ‘Across the Board,’ CEO Says After $4B Deal with Bayer
WRAL Techwire
October 26, 2020
Bayer Buys a Biotech ‘Race Horse’ with a $4B Deal — $2B in Cash — Aimed at Going Big into Gene Therapy
Endpoints News
September 22, 2020
Axovant Partners with Viralgen to Scale Production of Its AAV Gene Therapies
BioPharma Journal
August 12, 2020
Inc. 5000 2020: Introducing the 5,000 Fastest-Growing Private Companies in America
Inc. Magazine
August 3, 2020
From Science Fiction to Reality | Jude Samulski Honored in 2020 PharmaVOICE 100
PharmaVOICE
July 20, 2020
Researchers Hope Experimental Gene Therapy Is an Answer to a Fatal Genetic Disorder
7-minute listen
NPR | All Things Considered
June 24, 2020
Gene-editing Breakthrough? AskBio’s Jude Samulski Seeks Patent for New System
WRAL Techwire
April 28, 2020
AskBio Takes Over French Gene Therapy Company to Treat Alzheimer’s and Huntington’s
Labiotech EU
April 10, 2020
RTP-based AskBio Taps Former Histogenics Exec as New Chief Business Officer
WRAL Techwire
March 17, 2020
Big Pharma Shied Away from Gene Therapy for Years. Academia Picked Up the Slack.
BioPharma Dive
February 5, 2020
AskBio Initiates Phase I Trial of Gene Therapy for Heart Failure
Clinical Trials Arena
February 3, 2020
AskFirst: AskBio’s New Gene Therapy Program for Clinical Trial Patients
WRAL TechWire
December 19, 2019
Triangle-based AskBio to Pay up to $240M for Rights to Use Gene Therapy Technology
WRAL TechWire
December 3, 2019
2020: New Decade, New Disruption: Cell and Gene Therapy to Eradicate Genetic Diseases
Medical Expo
December 3, 2019
SQZ Biotech and AskBio Collaborate to Overcome AAV Immunogenicity
Manufacturing Chemist
October 24, 2019
Triangle Life Science Exec Sheila Mikhail Shines as ‘Northstar’ Award Winner
WRAL TechWire
August 23, 2019
Pfizer’s $500M investment in Sanford highlights NC’s growth in gene therapy
News & Observer
July 09, 2019
Cover Story: AskBio’s Tumultuous Ride to Achieve Unicorn Status
Triangle Business Journal
May 7, 2019
How This Promising Gene Therapy for a Rare Neuromuscular Disease Was Fueled by Passionate Parents and a Dog
Genetic Literacy Project
April 11, 2019
AskBio Reels in $235M to Ramp Up Gene Therapy Clinical Trials, Manufacturing
FierceBiotech
Let’s connect at an upcoming event. Check out the conferences and events we are attending and where we are speaking.
Upcoming Events
4th Annual Gene Therapy for Rare Disorders
Join us at the 4th Annual Gene Therapy for Rare Disorders conference, which will be held as a virtual event from February 22-25, 2021. AskBio’s Dr. David Favre will present “Immunotherapeutic Interventions” on Feb. 25 at 1:30pm ET.
BioProcess International U.S. West 2021
Andy Holt, EVP, Commercial Development, will present “Platform Development in AAV Manufacturing: Cost & Timeline Impact on Clinical Development” on March 30 (1:15-1:35pm PDT) at the BioProcess International U.S. West 2021 conference.
Past Events
9th Neurodegenerative Drug Development Summit
Join Dr. Krys Bankiewicz for the Emerging Gene Therapy Technology for Neurodegenerative Diseases workshop at the 9th Neurodegenerative Drug Development Summit on February 23, 2021.
WORLDSymposium 2021
AskBio is an exhibitor at WORLDSymposium 2021, which will be held as a virtual event from February 8-12, 2021.
RE(ACT) Congress & IRDiRC Conference
Join gene therapy expert Nathalie Cartier-Lacave for the Advanced Therapies panel at the RE(ACT) Congress & IRDiRC Conference, which will be held as a virtual meeting from January 13-15, 2021.
Biotech Showcase 2021
Join AskBio CEO and co-founder Sheila Mikhail and Marianne De Backer, EVP, Head of Strategy, Business Development & Licensing and Executive Committee Member at Bayer AG Pharmaceuticals, for an ON DEMAND fireside chat for insights on the recent acquisition.
2nd Annual Gene Therapy for Neurological Disorders
Jude Samulski will present at the 2nd Annual Gene Therapy for Neurological Disorders conference on Dec. 10, 2020.
Chief Medical Officer Summit 360
Join us at the 8th annual Chief Medical Officer Summit, the largest gathering of physicians in biotech, to be held virtually from October 26-27, 2020.
Cell & Gene Meeting on the Mesa
AskBio is a proud sponsor of the 2020 Cell & Gene Meeting on the Mesa. CEO Sheila Mikhail will deliver a pre-recorded company presentation that will be available on demand to registered attendees from October 12-16, 2020.
Chardan 4th Annual Genetic Medicines Conference
AskBio will present at the Chardan 4th Annual Genetic Medicines Conference, which will be held as a virtual event Oct 5-6, 2020.
Longwood Healthcare Leaders Forum – Fall 2020
AskBio CEO Sheila Mikhail will participate on a panel discussion among biopharmaceutical leaders at the Longwood Healthcare Leaders Forum on Monday, October 5, 2020.
Jefferies Gene Therapy/Editing Summit 2020
AskBio CEO Sheila Mikhail will present on Friday, Oct 2, from 10:30-10:55am ET at the Jefferies Gene Therapy/Editing Summit 2020, which will be held as a virtual meeting.
Morgan Stanley Global Healthcare Conference 2020
AskBio CEO Sheila Mikhail will participate in a fireside chat at the Morgan Stanley Virtual 18th Annual Global Healthcare Conference on Friday, September 18, 2020.
Advanced Therapies Congress 2020
Join AskBio Europe President David Venables for his presentation “Maximizing Value from the Expression Cassette in Gene Therapy Product Design” on Sept. 8.
The Bioprocessing Summit 2020
We’re presenting at the 12th Annual Bioprocessing Summit, which will be held virtually from Aug 24-28, 2020.
William Blair Biotech Focus Conference 2020
AskBio CEO Sheila Mikhail will participate in a fireside chat presentation at the William Blair Biotech Focus Conference, which will be held as a virtual event August 4-6, 2020.
The Art of Gene Therapy Digital Summit
Register today for The Art of Gene Therapy Digital Summit, a live two-day event on July 28-29, 2020, and join AskBio’s Andy Holt for the Next Decade of Gene Therapy panel on July 29, 11am-12pm ET.
Gene Therapy for Neurological Disorders Europe
We’re speaking at the Gene Therapy for Neurological Disorders Europe conference, which will be held as a virtual meeting on July 15, 2020. The conference unites industry leaders to help them overcome translational challenges and successfully bring CNS gene therapy candidates into the clinic.
BIO Digital 2020
Join us, the Buzz of BIO winner, for BIO Digital 2020. We have two on-demand sessions – our company presentation and “The Role of New Technologies in Enabling Cell & Gene Therapies” panel discussion.
Jefferies Virtual Healthcare Conference
AskBio CEO Sheila Mikhail will present at the Jefferies Virtual Healthcare Conference on June 2 from 9:30-9:55am. You can also download a copy of her presentation at this link.
Chardan 4th Annual Genetic Medicines Manufacturing Summit
Join AskBio’s Tim Kelly and Andy Holt on Tuesday, May 26, for Chardan’s 4th Annual Genetic Medicines Manufacturing Summit, which will be held in a virtual format this year.
ASGCT 2020 | Virtual Meeting
We’re looking forward to ASGCT 2020, which will be held May 12-15, 2020. We have a number of oral and poster presentations scheduled.
Meeting on the Med 2020 | Barcelona
Meeting on the Med 2020 has been canceled. It will be held April 7-9, 2021 in Barcelona.
OCT Southeast 2020 | Research Triangle Park, NC
OCT Southeast 2020 has been postponed. Stay tuned for new dates.
Gene Therapy in Edinburgh
This meeting has been postponed. A new date has not yet been scheduled.
2020 MDA Clinical & Scientific Conference | Orlando
This meeting has been postponed. A new date has not yet been scheduled.
CED Venture Connect 2020
CED has postponed the Venture Connect conference and will reschedule this event for a later date in 2020.
11th Open Scientific EIP Symposium on Immunogenicity of Biopharmaceuticals | Lisbon
Join David Favre, VP Translational Medicine, for “AAV Immunogenicity: Novel Vectors & New Questions” on Feb. 18, 10am.
Alliance for Regenerative Medicine (ARM) | 2020 Cell & Gene Therapies State of the Industry
AskBio CEO Sheila Mikhail joined gene therapy leaders for the Next-Generation Gene and Cell Technologies panel. [Video]
Springboard Enterprises’ 13th Annual Winners’ Circle Dinner
AskBio CEO Sheila Mikhail was recognized at Springboard Enterprises’ 13th Annual Winners’ Circle Dinner, as the 2019 Northstar honoree.
Chardan Genetic Medicines Conference
AskBio CEO Sheila Mikhail presented at the 3rd annual Chardan Genetic Medicines Conference in New York.
Cell & Gene Meeting on the Mesa
Sheila Mikhail, CEO, of AskBio presented our differentiating capabilities, technology and therapeutic pipeline.
National Limb Girdle Muscular Dystrophy Conference
Joy Carson and Sharon Hesterlee, joined patients, families and leading stakeholders at the first-annual National Limb Girdle Muscular Dystrophy Conference in support of the LGMD patient community in Chicago.
Parent Project Muscular Dystrophy, 25th Annual Conference
AskBio’s Jude Samulski and Sharon Hesterlee joined the 25th Parent Project Muscular Dystrophy in Orlando.
Gene Therapy Panel (Alliance for Regenerative Medicine)
AskBio’s Andy Holt, VP Business Development & Manufacturing, participated on the gene therapy panel at the Alliance for Regenerative Medicine meeting held in April 2019. [Video]
The Growing Promise of Gene Therapy Approaches
Josh Grieger, PhD, Chief Technology Officer at AskBio, presented “The Growing Promise of Gene Therapy Approaches” at an NIH-hosted meeting. [Video]
Media Inquiries
We take pride in our relationships with media representatives. Our scientific experts are always available if needed for interviews and their insights.
Media Contact:
Robin Fastenau, Vice President, Communications
