Expands AAV gene therapy platform from inside the cell for genetic disorders
Category: News
Viralgen Receives cGMP Certification from European Medicines Agency
Certification confirms Viralgen’s commitment to high operational standards with the world’s most flexible and robust AAV manufacturing capability
AskBio Applauds Pfizer’s Continuing Investments in Gene Therapy
New $500 million gene therapy manufacturing facility in North Carolina further validates AskBio’s groundbreaking AAV gene therapy accomplishments
AskBio Acquires Synpromics Ltd. and Expands its Gene Therapy Technology Portfolio
Synpromics to operate as a wholly owned subsidiary; the two companies bring together pioneering technology to increase efficacy of gene therapeutics
Selecta Biosciences Combines ImmTOR™ Platform with AskBio’s IndustryLeading Gene Therapy Platform in Strategic Partnership
Development pipeline and human trials planned for repeat dosing of AAV-based gene therapies to address the unmet medical need for patients with rare and orphan genetic diseases.
Statement: Pfizer Phase 1b Clinical Trial Results
Pfizer reported results from a Phase 1b clinical trial of PF-06939926, its investigational gene therapy for Duchenne Muscular Dystrophy (DMD).
Newly Approved Spinal Muscular Atrophy Gene Therapy, Zolgensma®, Validates AskBio Gene Therapy Platform
AskBio continues to lead the path for gene therapy development and cost-effective manufacturing methods based on the contributions of its co-founder, Dr. Jude Samulski
AskBio Partners with TPG and Vida Ventures
Leading gene therapy company announces $235 million investment to accelerate growth
First Patient Dosed with Gene Therapy in Phase 1/2 Study of ACTUS-101 in Patients with Pompe Disease
-Initial clinical study to evaluate ACTUS-101 over 52 weeks that could improve quality of life for those who are affected with rare genetic disorder – Pompe Disease.
Asklepios BioPharmaceutical, Inc. Launches New Portfolio Company – Actus Therapeutics, Inc.
Company will target rare genetic diseases including Pompe Disease
