Transforming medicine and changing lives

AskNews

June 28, 2021

AskBio Receives FDA Fast Track Designation for LION-101, a Novel Investigational AAV Gene Therapy for the Treatment of Limb-Girdle Muscular Dystrophy Type 2I/R9 (LGMD2I/R9)

AskBio announced that the U.S. Food & Drug Administration (FDA) has granted Fast Track Designation for the LION-101 gene therapy program. ...read the news

We are on a never-ending quest to advance genetic technology

and life-saving AAV gene therapy

In 1984, Dr. Jude Samulski, one of AskBio’s visionary founders, asked if a virus could be used to erase genetic disease. Discovering the answer cleared the path for historic advances in genetic medicine, and AskBio is leading the way.

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gene therapy

Revolutionizing gene therapy

Cures for life-altering diseases depend on new technology to lower the cost of treatment and increase supply for every patient who needs it.

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Clinical Pipeline

Changing lives

Our clinical pipeline is the direct result of listening to patients, their families, their care teams and disease-advocacy organizations.

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Putting patient care first

The voices of patients drive everything we do. They propel our research and the urgent need to find cures.

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Work with us

Advancing research

Today’s genetic discoveries are some of the most awe-inspiring advances in medical history. We welcome collaboration with innovative minds in genetic R&D.

Building careers

Help transform the face of healthcare with life-changing gene therapy. Every life enriched by our scientific advancements is a result of someone like you.

Events

Advanced Therapies Week

Jan 25

Jan 28

Advanced Therapies Week is the destination for anyone developers, investors or those interested in cell and gene therapies and tissue engineered products. Throughout the week, the organizers be host a variety of networking events, focused roundtables and content sessions designed to help biotechs advance along their commercialization journey.Speaker: Sheila Mikhail, CEO & Co-Founder, AskBioPresentation & Q&A Panel

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